ORTX(Delisted)
Orchard TherapeuticsยทNASDAQ
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ORTX Profile
Orchard Therapeutics Plc
A global gene therapy leader
245 Hammersmith Road, London W6 8PW, United Kingdom
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Orchard Therapeutics plc is a private limited liability company incorporated in England and Wales in August 2018. The company is a commercialized and fully integrated biopharmaceutical company dedicated to transforming serious life-threatening rare diseases through in vivo gene therapy. Their gene therapy approach aims to convert a patient's own or autologous HSC into a genetically modified drug product to treat the patient's disease with a single dose. They obtained this result by using a lentiviral vector to introduce a functional copy of the missing or defective gene into the patient's autologous HSC through an in vitro process, resulting in a drug product that can then be reintroduced into the patient at the bedside.
